Expert Speaker Faculty Commercial Strategy Andrew Komjathy Chief Commercial Officer Astria Therapeutics Jessica Gall Director Global Product Strategy BioMarin Pharmaceutical Liz Arnold Head of Commercial Strategy BridgeBio Pharma, Inc. Marsha Pelletier Global Pipeline & Business Development Commercial Strategy BioMarin Pharmaceutical Rebecca Derwin Global Commercial Lead – Gamifant Sobi HEOR – Health Economics and Outcomes Research Alejandro Cajigal Director - Real World Evidence Bristol Myers Squibb Jeffrey Yu Associate Director - HEOR Rare Disease Neurology Alexion Pharmaceuticals Michael Doane Senior Director- Head of HEOR Alkermes plc Sanket Shah Director Global Value HEOR Jazz Pharmaceuticals plc Vikram Patel Executive Director, HEOR field ACADIA Pharmaceuticals Inc. New Product Planning Carlos Eduardo Bertaglia Associate Medical Director, US New Product Planning Takeda Pharmaceutical Carole Gleeson Senior Director - New Product Planning & Portfolio Strategy Ventus Therapeutics Market Access and Pricing Adelpha Abrahamson Larkin Senior Director, Payer & Pricing Strategy Day One Biopharmaceuticals Inc. Bradley Armour Executive Director, US Immunology Sales & Marketing Sobi David Du Senior manager Market Access – Rare Disease Chiesi Liz Pfau Neurology Global Marketing Lead, Rare Disease Amgen Inc. Patient Education Betty Tran Executive Director, Head of Patient Services BridgeBio Pharma, Inc. Kathleen Gilluly Patient Education & Rare Disease Liaison Amicus Therapeutics, Inc. EVENT GUIDE REGISTER PARTNER